RARECast
Podcast tekijän mukaan RARECast - Torstaisin
548 Jaksot
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A Heart Attack that Led to a Rare Disease Diagnosis
Julkaistiin: 30.1.2025 -
Targeting Rare Liver Diseases with Gene Editing Therapies
Julkaistiin: 23.1.2025 -
Using AI to De-Risk Rare Disease Drug Development
Julkaistiin: 16.1.2025 -
Addressing a Growing Demand for Plasma-Derived Therapies
Julkaistiin: 9.1.2025 -
Empowering Patients with Data to Drive Drug Development
Julkaistiin: 2.1.2025 -
How Advocates Are Advancing a Treatment for an Ultra-Rare Disease
Julkaistiin: 26.12.2024 -
Engineering B Cells to Produce Therapeutic Proteins
Julkaistiin: 19.12.2024 -
A Pipeline Win as BridgeBio Learns to Balance Theory with Practice
Julkaistiin: 12.12.2024 -
Considering What It Will Take for Payers to Embrace Advances in Sequencing
Julkaistiin: 5.12.2024 -
Finding Strength
Julkaistiin: 27.11.2024 -
A Non-Profit Works to Advance a DMD Gene Therapy
Julkaistiin: 21.11.2024 -
Accepting What We Can’t Understand
Julkaistiin: 14.11.2024 -
A Gene Therapy Company Born from a Father’s Efforts to Save his Daughter
Julkaistiin: 7.11.2024 -
Lowering Barriers to Clinical Trial Participation with Do-It-Yourself Blood Sample Collection
Julkaistiin: 31.10.2024 -
Scaling N-of-1 Therapies to Viability
Julkaistiin: 24.10.2024 -
Building Gene Therapies that Address Gain and Loss of Function Simultaneously
Julkaistiin: 17.10.2024 -
How One Woman Climbed from Patient to Advocate
Julkaistiin: 10.10.2024 -
Shortening the Diagnostic Odyssey
Julkaistiin: 3.10.2024 -
Making Exomes More Revealing
Julkaistiin: 26.9.2024 -
How One Patient Organization Catalyzed Drug Development
Julkaistiin: 19.9.2024
RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy.
