RARECast
Podcast tekijän mukaan RARECast - Torstaisin
548 Jaksot
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Overcoming a Delivery Challenge of Retinal Gene Therapies
Julkaistiin: 19.6.2025 -
A Gene Editing First Augurs an Era of Bespoke Therapies
Julkaistiin: 12.6.2025 -
How One Patient Organization Drives Drug Development
Julkaistiin: 5.6.2025 -
Using CRISPR to Modulate Gene Expression
Julkaistiin: 29.5.2025 -
Satisfying the Hunger for a Prader-Willi Therapy
Julkaistiin: 22.5.2025 -
How an Academic Medical Center Helped Change the Landscape for a Rare Disease
Julkaistiin: 15.5.2025 -
Improving Outcomes for People with a Set of Rare Cancers
Julkaistiin: 8.5.2025 -
An Effort to Build a Better DMD Gene Therapy
Julkaistiin: 2.5.2025 -
A Once-Failed Pain Therapy Shows Potential in a Neurodevelopmental Disorder
Julkaistiin: 24.4.2025 -
Advancing a Cutting-Edge Therapy for a Rare, Childhood Cancer
Julkaistiin: 17.4.2025 -
Learning to Take His Vitamins
Julkaistiin: 10.4.2025 -
The First Treatment for a Rare Neurodegenerative Condition Awaits FDA Approval
Julkaistiin: 3.4.2025 -
Engineering Skin Bacteria to Be Live Biotherapeutics
Julkaistiin: 27.3.2025 -
Seeing the Gene and Cell Therapy Translational Divide as an Opportunity
Julkaistiin: 20.3.2025 -
My Mother, Myself, and ALS
Julkaistiin: 13.3.2025 -
From Immovable Object to Advocacy Force
Julkaistiin: 6.3.2025 -
A Rapid and Scalable Approach for Screening Personalized ASOs
Julkaistiin: 27.2.2025 -
Addressing the Disease Mechanism of a Rare Kidney Disease
Julkaistiin: 20.2.2025 -
The Mother of a Son with SCD, Applies Direct Experience to Her Clinical Trials Work
Julkaistiin: 13.2.2025 -
A First for Rett Syndrome with More in the Pipeline
Julkaistiin: 6.2.2025
RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy.
